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Gaucher disease is a rare inherited metabolic disorder caused by the deficiency of the enzyme glucocerebrosidase. This, in turn, causes the accumulation of certain detrimental lipids in the body, especially the glycolipid glucocerebroside. The lipids are accumulated mainly within the macrophages, blood cells, spleen, liver, and bone marrow. Approximately 34 genetic mutations have been identified that leads to Gaucher disease, out of which there are four most prominent mutations that lead to more than half of the Gaucher disease globally. Some people may have no symptoms of this disease, while some experience severe complications. Some of the clinical manifestations of this disease are hepatosplenomegaly, anemia, thrombocytopenia, and skeletal abnormalities. According to the Gaucher disease industry analysis, Technavio's analysts predict this market to grow at a CAGR of 7.60 percent over the period 2014-2019.
This report covers the present scenario and the growth prospects of the Global Gaucher Disease market for the period 2015-2019. To calculate the Gaucher disease market size & share, the report considers revenue from the sales of various drugs used in the therapy of Gaucher disease, which includes:
• Enzyme replacement therapy
• Substrate reduction therapy
• Biologics
• Small Molecules
• Oral
• Parenteral
• Solid
• Liquid
01. Executive Summary
02. List of Abbreviations
03. Scope of the Report
03.1 Market Overview
03.2 Product Offerings
04. Market Research Methodology
04.1 Market Research Process
04.2 Research Methodology
05. Introduction
06. Disease Overview
06.1 Understanding the Disease
06.1.1 Types of Gaucher Disease
06.1.2 Symptoms
06.1.3 Diagnosis
06.2 Etiology
06.3 Epidemiology
06.4 Clinical Manifestations
06.5 Management
06.5.1 Enzyme Replacement Therapy
06.5.2 Substrate Reduction Therapy
06.6 Economic Burden
07. Pipeline Analysis
08. Market Landscape
08.1 Market Overview
08.2 Market Size and Forecast
08.3 Five Forces Analysis
09. Market Segmentation by Type of Therapy
09.1 Enzyme Replacement Therapy
09.2 Substrate Reduction Therapy
10 Market Segmentation by Type of Molecule
10.1 Biologics
10.2 Small Molecules
11 Market Segmentation by Route of Administration
11.1 Oral
11.2 Parenteral
12 Market Segmentation by Dosage Form
12.1 Solid
12.2 Liquid
13 Geographical Segmentation
14 Buying Criteria
15 Market Growth Drivers
16 Drivers and their Impact
17 Market Challenges
18 Impact of Drivers and Challenges
19 Market Trends
20 Trends and their Impact
21 Vendor Landscape
21.1 Competitive Scenario
21.1.1 Key News
21.1.2 Mergers and Acquisitions
21.2 Market Share Analysis 2014
21.2.1 Genzyme
21.2.2 Shire
21.2.3 Actelion Pharmaceuticals
21.2.4 Pfizer
21.3 Other and Future Prominent Vendors
22 Key Vendor Analysis
22.1 Actelion Pharmaceuticals
22.1.1 Key Facts
22.1.2 Business Overview
22.1.3 Geographical Segmentation 2013
22.1.4 Business Strategy
22.1.5 Recent Developments
22.1.6 SWOT Analysis
22.2 Genzyme
22.2.1 Key Facts
22.2.2 Business Overview
22.2.3 Product Segmentation by Revenue 2013
22.2.4 Product Segmentation by Revenue 2012 and 2013
22.2.5 Geographical Segmentation
22.2.6 Business Strategy
22.2.7 Recent Developments
22.2.8 SWOT Analysis
22.3 Pfizer
22.3.1 Key Facts
22.3.2 Business Overview
22.3.3 Business Segmentation by Revenue 2013
22.3.4 Business Segmentation by Revenue 2012 and 2013
22.3.5 Geographical Segmentation by Revenue
22.3.6 Business Strategy
22.3.7 Key Developments
22.3.8 SWOT Analysis
22.4 Shire
22.4.1 Key Facts
22.4.2 Business Overview
22.4.3 Geographical Segmentation by Revenue 2013
22.4.4 Business Strategy
22.4.5 Recent Developments
22.4.6 SWOT Analysis
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